Gene therapy is the insertion of genes into an individual's cells and tissues to treat a disease, and hereditary diseases in particular. Gene therapy typically aims to supplement a defective mutant allele with a functional one.
Gene Therapy III
Most of the approaches to gene therapy attempted to date — and described in other pages — involve the use of vectors to introduce a functioning gene into cells.
Gene Therapy Clinical Trials
Gene therapy studies in ClinicalTrials.gov - The U.S. National Institutes of Health resource for public access to information on clinical research studies.
Gene Therapy
Gene therapy is an experimental technique for treating disease by altering the patient's genetic material. Most often, gene therapy works by introducing a healthy copy of a defective gene into the patient's cells.
Beyond gene therapy
As mentioned at the outset of this article, the revolution in human genetics will extend beyond identifying and preventing or treating genetic ailments.
gene therapy The insertion of normal or genetically altered genes into cells through the use of recombinant DNA technology; usually done to replace defective genes as part of the treatment of genetic disorders.
Gene therapy: a newly evolving technique used to treat inherited genetic diseases. The medical procedure involves substituting the defective gene in the cells of a patient's body with a healthy gene.
Gene therapy
An evolving technique used to treat inherited diseases. The medical procedure involves replacing, manipulating, or supplementing non-functional genes with healthy genes, in order to affect their function. [Talking Glossary] ...
Gene Therapy
Gene therapy uses technology to change the genetic composition of a cell.
Ex vivo ...
[edit] Gene Therapy
Main article: Gene therapy
Many mutations in a person's genes result in severe medical condition.
Gene therapy is a more ambitious endeavor: its goal is to treat or cure a disease by providing a normal copy of the individual's mutated gene.
Human gene therapy
Insertion of normal DNA directly into cells to correct a genetic defect.
Related Terms:
Single-gene disorder
Hereditary disorder caused by a mutant allele of a single gene (e.g.
Somatic cell gene therapy. The repair or replacement of a defective gene within somatic tissue. (See Somatic cell.)
Somatotrophin. See Human growth hormone.
Southern blotting. See Southern hybridization.
Germ cell (germ line) gene therapy. The repair or re- placement of a defective gene within the gamete-forming tissues, which produces a heritable change in an organism's genetic constitution. GMO. Genetically modified organism. Green revolution.
Gene therapy -- addition of a functional gene or group of genes to a cell by gene insertion to correct an hereditary disease.
Recombinant DNA technology is important for learning about other related technologies, such as gene therapy, genetic engineering of organisms, and sequencing genomes.
Newborn and Carrier Screening and Gene Therapy
T Ch 13, 14, 20
PKU, galactosemia, sickle cell, hypothyroidism; Tay-Sachs, hemoglobinopathies, cystic fibrosis. Enzyme replacement and gene therapy.
Affected individuals suffer from a series of seemingly minor infections and usually die at an early age. A small group suffering from adenosine deaminase (ADA) deficiency, a type of SCID, are undergoing gene therapy to provide them with normal ...
 See also: Human, Trans, DNA, Organ, Gene
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